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Sabrina Paille


Sabrina Paille

Senior Medical Director , Audentes Therapeutics, Switzerland

Biography

Sabrina Paillé is a Senior Medical Director in the Clinical Development Department within Audentes Therapeutics, an Astellas company. She completed her Medical Degree at age 23 from the M. Mammeri University of Medicine, in Algeria. Sabrina has over 20 years of experience in pharmaceutical industry working in rare neuromuscular disorders (SMA, XLMTM, DMD and Pompe Disese), with extensive knowledge in the application of antisense oligonucleotides and AAV-based gene therapy to treat genetic diseases.

 

 

Abstract

Abstract : ASPIRO Gene Therapy Trial In X-Linked Myotubular Myopathy (XLMTM): Update on Preliminary Safety And Efficacy Findings up to 72 Weeks Post-Treatment